Category Archives: Therapy, Treatment & Research

Medical Research: Discovery, Translational, Clinical [in plain English]

by Elizabeth Halford, with contributions from Steve Kaminsky, Ph.D. Janice Ascano, Ph.D., Paige Nues and Kori Coates. There are three streams of scientific research into Rett syndrome: discovery based research, treatment (“translational”) based research and clinical research. IRSF have an ongoing study into Rett syndrome via their Natural History Study which is a fantastic form of clinical research. We’d...

Gene therapy for Rett syndrome?

by Elizabeth Halford, with contributions from Steve Kaminsky, Ph.D., Janice Ascano, Ph.D., Paige Nues, Monica Coenraads and Kori Coates. As of late, there’s been much buzz about gene therapy as a potential treatment  for Rett syndrome. And for good reason! Gene therapy isn’t new. In fact, it’s been used to treat a number of disorders, among them: retinal disease, acute...

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